Are There Any New Treatments For ATTR Transthyretin On The Horizon?
Yes, NI006 and PRX004 antibody drugs. They are depleter drugs. There are others undergoing clinical trials. Also CRIPR-Cs9 gene editing
a 1 time ininfusion treatment that totally eliminates production of liver production of thyretin.
Thanks so much for that info on new treatments. Hope Columbia Amyloidosis Center knows about them. I will have toask them because my next appointment isn't for a couple of months.
You are welcome! I'm certain that Columbia Amyloidosis Center is up-to-date date on all of the clinical trials for depleter drugs.
Cardiac Hereditary Amyloidosis
Have You Found Vyndamax To Help Or Shortness Of Breath Or Relieve It Altogether? Has Helped Me But I Still Get Winded Walking.
Hello….Those Of You With Hattr. Did It Tend To Run In Your Families? And Was The Age Of Onset Younger Than 75?